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Clinical Trials on X-bundet adrenoleukodystrofi in United Kingdom
Totalt 1618 resultater
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Great Ormond Street Hospital for Children NHS Foundation...TilbaketrukketGranulomatøs sykdom, kronisk, X-bundet, variantStorbritannia
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National Institute of Allergy and Infectious Diseases...UkjentX-koblede kombinerte immunsviktsykdommerForente stater
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National Institute of Allergy and Infectious Diseases...FullførtAlvorlig kombinert immunsviktForente stater
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Healx LimitedTilbaketrukketFragilt X-syndromForente stater, Australia
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Rett Syndrome Research TrustFullført
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Hugo W. Moser Research Institute at Kennedy Krieger...Avsluttet
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Eunice Kennedy Shriver National Institute of Child...UkjentRett syndromForente stater
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Jazz PharmaceuticalsAvsluttetRett syndrom | RTTForente stater, Spania, Italia, Storbritannia
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Stanford UniversityFullførtIntellektuell funksjonshemming | Fragilt X-syndromForente stater
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Seaside Therapeutics, Inc.FullførtFragilt X-syndromForente stater
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Tetra Discovery PartnersRekrutteringFragilt X-syndromForente stater
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Tetra Discovery PartnersPåmelding etter invitasjonFragilt X-syndromForente stater
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Neurogene Inc.RekrutteringRett syndromForente stater
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National Human Genome Research Institute (NHGRI)FullførtRett syndromForente stater
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Neuren Pharmaceuticals LimitedFullført
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationFullført
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital... og andre samarbeidspartnereRekruttering
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgFullført
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Seaside Therapeutics, Inc.FullførtFragilt X-syndromForente stater
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Seaside Therapeutics, Inc.Avsluttet
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SwanBio Therapeutics, Inc.RekrutteringAMN | AMN-genmutasjon | X-ALDNederland, Forente stater
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Rett Syndrome Research TrustVanderbilt University Medical CenterFullført
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Indiana UniversityFullførtFragilt X-syndrom | AutismespekterforstyrrelserForente stater
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ACADIA Pharmaceuticals Inc.FullførtRett syndromForente stater
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ACADIA Pharmaceuticals Inc.FullførtRett syndromForente stater
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ACADIA Pharmaceuticals Inc.Fullført
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University of North Carolina, Chapel HillFullførtFragilt X-syndrom | Psykose | AutismespekterforstyrrelserForente stater
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbeidspartnereRekruttering
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Edison Pharmaceuticals IncTilbaketrukket
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University of South FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbeidspartnereFullført
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Hugo W. Moser Research Institute at Kennedy Krieger...The Johns Hopkins Institute for Clinical and Translational Research (ICTR)FullførtRett syndromForente stater
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Boston Children's HospitalInternational Rett Syndrome FoundationFullført
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The Cleveland ClinicAvsluttet
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Boston Children's HospitalAutism Speaks; International Rett Syndrome FoundationFullført
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Stanford UniversityAvsluttetFragilt X-syndrom (FXS) | Idiopatisk intellektuell utviklingsforstyrrelse (IDD)Forente stater
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Ovid Therapeutics Inc.Fullført
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForente stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Astellas Gene TherapiesFullførtMenn med X-koblet myotubulær myopati (XLMTM)Forente stater, Storbritannia
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National Institute of Allergy and Infectious Diseases...FullførtGenetiske sykdommer, X-linked | Lymfoproliferativ sykdom | X-koblet lymfoproliferativ sykdomForente stater
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REGENXBIO Inc.FullførtMukopolysakkaridose IIBrasil, Forente stater, Storbritannia
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkjent
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbeidspartnereRekruttering
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RekrutteringRett syndrom | Rett syndrom, atypisk | RTTForente stater
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Masonic Cancer Center, University of MinnesotaTilbaketrukket
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)AvsluttetAdrenoleukodystrofi | AdrenomyeloneuropatiForente stater
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Edimer PharmaceuticalsFullførtX-koblet Hypohidrotisk ektodermal dysplasi | Hypohidrotisk ektodermal dysplasiForente stater
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUkjentWiskott-Aldrich syndrom | Leukocyttadhesjonsmangelsyndrom | X-koblet agammaglobulinemi | X-Linked Hyper IgM SyndromeForente stater
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Neuren Pharmaceuticals Limitedrettsyndrome.orgFullført
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Nido Biosciences, Inc.RekrutteringSpinal og Bulbar muskelatrofi | Kennedys sykdomKorea, Republikken, Danmark, Italia, Storbritannia