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Kliniske forsøg med X-Linked Dystoni Parkinsonisme
I alt 1608 resultater
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Applied Genetic Technologies CorpAfsluttetX-Linked Retinitis PigmentosaForenede Stater
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Eunice Kennedy Shriver National Institute of Child...RekrutteringAutismespektrumforstyrrelse | Fragilt X syndrom | Udviklingsforsinkelse | Genetisk lidelse | Asperger lidelseForenede Stater
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetRett syndrom | CDKL5 lidelse | MECP2 Duplikationslidelse | FOXG1 syndromForenede Stater
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Janssen Pharmaceutical K.K.RekrutteringX-Linked Retinitis PigmentosaJapan
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Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University og andre samarbejdspartnereRekrutteringX-Linked Retinitis PigmentosaKina
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Janssen Pharmaceutical K.K.AfsluttetX-Linked Retinitis PigmentosaJapan
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Janssen Research & Development, LLCJanssen Research & Development, LLCAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaBelgien, Canada, Forenede Stater, Israel, Det Forenede Kongerige, Spanien, Danmark, Frankrig, Italien, Holland, Schweiz
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Ariel UniversityASST Santi Paolo e CarloAfsluttet
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Bambino Gesù Hospital and Research InstituteAutour Des Williams; AceaUkendtFragilt X syndrom | Williams syndromItalien
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University Hospital, MontpellierAssociation Xtraordinaire sub-group DDX3X; GenidaUkendtIntellektuel udviklingsforstyrrelse | X-LINKEDFrankrig
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Beacon TherapeuticsRekruttering
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Beacon TherapeuticsAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater
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Beacon TherapeuticsAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater
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Beacon TherapeuticsTilmelding efter invitationX-Linked Retinitis PigmentosaForenede Stater
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Janssen Research & Development, LLCAktiv, ikke rekrutterendeX-Linked Retinitis PigmentosaForenede Stater, Det Forenede Kongerige
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Rare Thyroid Therapeutics International ABVitaccess LtdAfsluttetAllan-Herndon-Dudley syndrom | Monocarboxylat Transporter 8 (MCT8) mangelDet Forenede Kongerige
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National Institute of Allergy and Infectious Diseases...AfsluttetImmunproliferativ lidelseForenede Stater
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRekrutteringMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater, Det Forenede Kongerige, Holland
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University of California, San FranciscoMRI Interventions, Inc.AfsluttetParkinsons sygdom | DystoniForenede Stater
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University of California, Los AngelesThe Dana FoundationUkendtParkinsons sygdom | Ataksi | DystoniForenede Stater
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Baylor College of MedicineAfsluttet
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Ionis Pharmaceuticals, Inc.Ikke rekrutterer endnuMethyl CpG Binding Protein 2 (MECP2) Duplikationssyndrom
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Assistance Publique - Hôpitaux de ParisBraintaleIkke rekrutterer endnuX-bundet adrenoleukodystrofi
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W... og andre samarbejdspartnereAfsluttetX-bundet adrenoleukodystrofiForenede Stater
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Shenzhen Geno-Immune Medical InstituteUkendt
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NeuroVia, Inc.Trukket tilbageX-forbundet adrenoleukodystrofiAustralien, Argentina, Det Forenede Kongerige, Colombia, Chile, Frankrig, Den Russiske Føderation, Ukraine
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Beijing Tiantan HospitalRekruttering
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University of MinnesotaIkke længere tilgængeligX-bundet adrenoleukodystrofiForenede Stater
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationAfsluttetAdrenomyeloneuropati | X-bundet adrenoleukodystrofiHolland
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Rutgers, The State University of New JerseyRekrutteringParkinsons sygdom | Bevægelsesforstyrrelser | Huntingtons sygdom | Essential Tremor | Spinocerebellære ataksier | Dystoni, PrimærForenede Stater
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University... og andre samarbejdspartnereRekrutteringSygdomme i nervesystemet | Neurologiske manifestationer | Neuroadfærdsmæssige manifestationer | Genetiske sygdomme, X-forbundet | Intellektuel handicap | Neuroudviklingsforstyrrelser | Neurologisk lidelse | Rett syndrom | Genetisk sygdom | Rett syndrom, atypiskForenede Stater
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Universitair Ziekenhuis BrusselMarguerite - Marie Delacroix FoundationIkke rekrutterer endnuKlassiske lissencefalier og subkortikale båndheterotoperBelgien
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationAfsluttetAdrenomyeloneuropati | X-bundet adrenoleukodystrofiSpanien
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationAfsluttetX-bundet adrenoleukodystrofiForenede Stater
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University of OxfordIkke rekrutterer endnuParkinsons sygdom | Dystoni | RystenDet Forenede Kongerige
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Centre Hospitalier Universitaire de NiceAfsluttetParkinsons sygdom | Dystoni | RystenFrankrig
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New York Institute of TechnologyAfsluttetParkinsons sygdom | Dystoni | Autonom dysrefleksiForenede Stater
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Ionis Pharmaceuticals, Inc.RekrutteringMethyl CpG Binding Protein 2 (MECP2) DuplikationssyndromForenede Stater
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxLedigMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater
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NightstaRx Ltd, a Biogen CompanyAfsluttetX-Linked Retinitis PigmentosaForenede Stater, Frankrig, Det Forenede Kongerige, Finland, Holland, Tyskland, Canada
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University Hospital, GrenobleTrukket tilbageParkinsons sygdom | OCD | Dystoni
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University Health Network, TorontoRekrutteringParkinsons sygdom | Dystoni | Essential TremorCanada
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Massachusetts General HospitalRekrutteringParkinsons sygdom | Dystoni | Essential TremorForenede Stater
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Mayo ClinicAfsluttetParkinsons sygdom | Dystoni | Essential TremorForenede Stater
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University Children's Hospital, ZurichAfsluttetParkinsons sygdom | Dystoni | Essential TremorSchweiz
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Vanderbilt UniversityTrukket tilbageParkinsons sygdom | Dystoni | Essential TremorForenede Stater
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University of California, DavisEunice Kennedy Shriver National Institute of Child Health and Human Development...Tilmelding efter invitationIntellektuel handicap | Downs syndrom | Attention Deficit Hyperactivity Disorder | Fragilt X syndromForenede Stater
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbejdspartnereAfsluttetRett syndrom, bevaret talevariant | Mecp2 duplikationssyndrom | Rett-relaterede lidelserForenede Stater
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National Institute of Neurological Disorders and...AfsluttetParkinsons sygdom | Dystoni | Essential TremorForenede Stater
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All India Institute of Medical Sciences, New DelhiIkke rekrutterer endnu