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Søg i kliniske forsøg efter: Lysosomal Storage Diseases, Nervous System
I alt 248699 resultater
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GeneCradle IncRekrutteringPompes sygdom (sen debut)Kina
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Lundquist Institute for Biomedical Innovation at...Ikke rekrutterer endnuMucopolysaccharidosis III | Sanfilippo syndromForenede Stater
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Chiesi Farmaceutici S.p.A.ICON plcIkke rekrutterer endnu
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Caroline Michaela KistorpSanofiIkke rekrutterer endnuKroniske nyresygdomme | Fabrys sygdomDanmark
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National Taiwan University HospitalRekruttering
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Forge Biologics, IncIkke rekrutterer endnuKrabbes sygdomForenede Stater
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RekrutteringType II Gauchers sygdomKina
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UniQure Biopharma B.V.RekrutteringFabrys sygdomForenede Stater
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRekruttering
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Chung-Hsing WangSanofiIkke rekrutterer endnu
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University of CambridgeSanofiRekrutteringFabrys sygdom, hjertevariantDet Forenede Kongerige
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Children's Hospital of Fudan UniversityIkke rekrutterer endnu
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SanofiPulse Infoframe Ltd.RekrutteringNiemann-Pick Sygdomme | Syre sphingomyelinase mangelForenede Stater
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Huashan HospitalIkke rekrutterer endnuPompes sygdom (sen debut)Kina
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Qilu Hospital of Shandong UniversityRekrutteringFabrys sygdom | Hypertrofisk kardiomyopati | Venstre ventrikulær hypertrofiKina
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He HuangLingyi Biotech Co., Ltd.Rekruttering
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Astellas Gene TherapiesRekrutteringPompes sygdom (sen debut)Forenede Stater, Spanien, Frankrig, Taiwan, Italien, Australien
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McMaster UniversityIkke rekrutterer endnuFedme | Lysosomale opbevaringssygdomme | Muskeltab | Glykogenopbevaringssygdom type II | Pompes sygdom | Dårlig ernæring | Glykogenopbevaringssygdom type II, voksen | Glykogenopbevaring Sygdom type II sent indtræden
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Amicus TherapeuticsRekrutteringPompes sygdomForenede Stater, Det Forenede Kongerige, Tyskland
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Lysosomal and Rare Disorders Research and Treatment...RekrutteringKnoglesygdomme | Gauchers sygdomForenede Stater
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AceLink Therapeutics, Inc.Tigermed Consulting Co., LtdRekruttering
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Rocket Pharmaceuticals Inc.RekrutteringDanons sygdomForenede Stater
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Westfälische Wilhelms-Universität MünsterChiesi GmbHRekruttering
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ISU Abxis Co., Ltd.RekrutteringFabrys sygdomKorea, Republikken
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UK Kidney AssociationRekrutteringVaskulitis | AL Amyloidose | Tuberøs sklerose | Fabrys sygdom | Cystinuri | Fokal Segmental Glomerulosklerose | IgA nefropati | Bartter syndrom | Pure Red Cell Aplasia | Membranøs nefropati | Atypisk hæmolytisk uræmisk syndrom | Autosomal dominant polycystisk nyresygdom | Cystinose | Nephronophthisis | BK nefropati | Calcip... og andre forholdDet Forenede Kongerige
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Lysosomal and Rare Disorders Research and Treatment...Rekruttering
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SanofiRekruttering
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Institut National de la Santé Et de la Recherche...RekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multipel Sulfatase mangel sygdom | Mucopolysaccharidosis IXFrankrig
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TakedaRekrutteringHunters syndromCanada, Frankrig
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SanofiRekrutteringFabrys sygdomForenede Stater
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaRekruttering
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Fundación Española de Hematología y HemoterapíaRekrutteringGauchers sygdom | Syre SphingoMyelinase mangelSpanien
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Fondazione Don Carlo Gnocchi OnlusAssociazione Italiana Glicogenosi (AIG); Associazione Riabilitatori Insufficienza... og andre samarbejdspartnereRekrutteringGlykogenopbevaringssygdom type II | Pompes sygdom (sen debut)Italien
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Medical University of ViennaRekrutteringPompes sygdom | McArdles sygdomØstrig
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Hospices Civils de LyonRekruttering
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Eline C. B. EskesRekruttering
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Eline C. B. EskesRekruttering
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Bio Sidus SARekruttering
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University of MinnesotaRekrutteringGauchers sygdomForenede Stater
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Assiut UniversityIkke rekrutterer endnu
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GeneCradle IncRekrutteringPompes sygdom infantilKina
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Massachusetts General HospitalRekruttering
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Fondazione Policlinico Universitario Agostino Gemelli...Rekruttering
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Forge Biologics, IncRekrutteringKrabbes sygdomForenede Stater
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SanofiRekruttering
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Albina Nowak, MDIkke rekrutterer endnu
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Chiesi Farmaceutici S.p.A.ICON plcRekruttering
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Mackay Memorial HospitalRekruttering
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Children's Hospital Medical Center, CincinnatiSanofiRekrutteringFabrys sygdomForenede Stater