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Søg i kliniske forsøg efter: Lysomale Speicherkrankheit
I alt 945 resultater
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University of MinnesotaRekrutteringGauchers sygdomForenede Stater
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Cystinose StiftungScreening Laboratory Hannover; Pediatry Kastanienhof Koeln; Medical Genetics... og andre samarbejdspartnereRekrutteringCystinose | Primær hyperoxaluriTyskland
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudIkke rekrutterer endnuSanfilippo syndrom type CForenede Stater, Frankrig
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Assiut UniversityIkke rekrutterer endnu
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GeneCradle IncRekrutteringPompes sygdom infantilKina
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Massachusetts General HospitalRekruttering
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Fondazione Policlinico Universitario Agostino Gemelli...Rekruttering
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Forge Biologics, IncRekrutteringKrabbes sygdomForenede Stater
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SanofiRekruttering
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Albina Nowak, MDIkke rekrutterer endnu
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Chiesi Farmaceutici S.p.A.ICON plcRekruttering
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRekrutteringSanfilippo syndrom | MPS3Forenede Stater
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Mackay Memorial HospitalRekruttering
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Children's Hospital Medical Center, CincinnatiSanofiRekrutteringFabrys sygdomForenede Stater
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier... og andre samarbejdspartnereRekrutteringMedfødt binyrehyperplasi | Hæmofili A | Hæmofili B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystisk fibrose | Alpha 1-Antitrypsin mangel | Seglcellesygdom | Fanconi Anæmi | Kronisk granulomatøs sygdom | Wilsons sygdom | Svær medfødt neutropeni | Ornithin Transcarbamylase mangel | Mucopolysaccharidosis VI | Lysosomal... og andre forholdBelgien
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Immusoft of CA, Inc.RekrutteringMucopolysaccharidosis IH/S | Mucopolysaccharidosis ISForenede Stater
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Yonsei UniversityRekrutteringFabrys sygdomKorea, Republikken
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TakedaIkke rekrutterer endnu
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital... og andre samarbejdspartnereRekruttering
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Eunice Kennedy Shriver National Institute of Child...RekrutteringNiemann-Pick sygdom type C1 | Juvenil neuronal ceroid lipofuscinose | Smith-Lemli-Opitz syndrom | Kreatin Transporter mangelForenede Stater
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Fundación Española de Hematología y HemoterapíaRekrutteringNiemann-Pick Sygdomme | Gauchers sygdom | Splenomegali | Syre SphingoMyelinase mangel | ASMDSpanien
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Masonic Cancer Center, University of MinnesotaRekrutteringMucopolysaccharidosis type I | Hæmatopoietisk celletransplantationForenede Stater
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University of California, San FranciscoRekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolmans sygdom | Pompes sygdom infantil | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopatisk Gauchers sygdomForenede Stater
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Eunice Kennedy Shriver National Institute of Child...RekrutteringNiemann-Pick sygdom, type CForenede Stater
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University of MinnesotaRekrutteringGauchers sygdom, type 3Forenede Stater
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRekruttering
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Assistance Publique - Hôpitaux de ParisCystinosis Research FoundationRekruttering
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New York Stem Cell Foundation Research InstituteSilverstein FoundationRekrutteringSund og rask | Parkinsons sygdom | Gauchers sygdom | GBA-genmutationForenede Stater
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Sanguine BiosciencesDenali Therapeutics Inc.RekrutteringMucopolysaccharidosis III-AForenede Stater
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Alice BertainaCalifornia Institute for Regenerative Medicine (CIRM)RekrutteringCKD trin 4 | Cystinose | FSGS | SLE nefritis | SIODForenede Stater
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TakedaTakeda Development Center Americas, Inc.RekrutteringHunters syndrom | Mucopolysaccharidosis (MPS)Forenede Stater
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Prevail TherapeuticsEli Lilly and CompanyRekrutteringGauchers sygdom | Gauchers sygdom, type 1Forenede Stater, Spanien, Tyskland
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National Taiwan University HospitalRekrutteringSlag | MR scanning | Fabrys sygdom | Cerebrale småkarsygdomme | Cadasil | HTRA1-relateret autosomal dominant cerebral angiopati | COL4A1-relateret hjernens lille karsygdom med blødning | Næste generations sekvenseringTaiwan
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CANbridge (Suzhou) Bio-pharma Co., Ltd.RekrutteringGauchers sygdom, type 1 | Gauchers sygdom, type 3Kina
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Centre for Analytical Biochemistry and Biomedical...University of GiessenRekruttering
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Duke UniversityGenzyme, a Sanofi CompanyRekrutteringSent-debuterende Pompes sygdom | Lysosomal sygdomForenede Stater
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GC Biopharma CorpRekrutteringMucopolysaccharidosis II | Hunters syndromKorea, Republikken
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University of Roma La SapienzaAlexion PharmaceuticalsRekrutteringIkke-alkoholisk fedtleversygdomItalien
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Academisch Medisch Centrum - Universiteit van Amsterdam...Rekruttering
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Universidade do PortoHospital da Luz, Lisboa; Hospital Pedro Hispano; Centro Hospitalar de Leiria og andre samarbejdspartnereRekruttering
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Denali Therapeutics Inc.RekrutteringMucopolysaccharidosis IIForenede Stater, Spanien, Det Forenede Kongerige, Tjekkiet, Frankrig, Canada, Italien, Belgien, Holland, Tyskland, Argentina, Sverige, Kalkun, Colombia, Brasilien
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SanofiRekrutteringAcid Sphingomyelinase Deficiency (ASMD)Frankrig
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Manchester University NHS Foundation TrustOrchard TherapeuticsRekrutteringMucopolysaccharidoserDet Forenede Kongerige
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Freeline TherapeuticsRekrutteringGauchers sygdom, type 1Spanien, Israel, Forenede Stater, Det Forenede Kongerige, Brasilien, Tyskland, Paraguay
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringMucopolysaccharidosis IV Type A | Morquio A syndrom | MPS IVAForenede Stater
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SanofiRekrutteringFabrys sygdomItalien, Forenede Stater, Østrig, Kina, Tjekkiet, Danmark, Frankrig, Tyskland, Grækenland, Japan, Korea, Republikken, Holland, Norge, Spanien, Taiwan, Kalkun, Det Forenede Kongerige, Canada, Polen
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LMU KlinikumRekrutteringPompes sygdom (sen debut) | FSHD | Spinal muskelatrofi type 3 | Inclusion Body MyositisTyskland
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Shaare Zedek Medical CenterRekruttering
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SanofiRekrutteringGauchers sygdom type IIIForenede Stater, Tyskland, Ungarn, Frankrig, Kina, Japan, Canada, Argentina, Italien, Kalkun
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AO GENERIUMRekrutteringMetaboliske sygdomme | Mucopolysaccharidosis Type IIDen Russiske Føderation