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Søg i kliniske forsøg efter: Congenital myasthenic syndrome
I alt 44347 resultater
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River 3 Renal Corp.RekrutteringFokal Segmental Glomerulosklerose | Alport syndromForenede Stater, Belgien, Det Forenede Kongerige, Frankrig, Tyskland, Holland
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Zhejiang UniversityYake Biotechnology Ltd.RekrutteringVaskulitis | Amyloidose | Autoimmun hæmolytisk anæmi | DIGTE syndromKina
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Novartis PharmaceuticalsRekruttering
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Assistance Publique - Hôpitaux de ParisRekruttering
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RekrutteringMyelodysplastiske syndromer | Primære immundefektsygdomme | Hæmoglobinopatier | Kronisk myeloid leukæmi | Cytopeni | Alvorlig aplastisk anæmi | Knoglemarvsfejlsyndrom | Akut myeloid leukæmi i remission | Hæmofagocytiske lymfohistiocytoser | Akut lymfatisk leukæmi i remission | Alvorlig kronisk aktiv Epstein-Barr-virusinfektionForenede Stater
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Cairo UniversityRekrutteringIndfangningsneuropatierEgypten
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Vanderbilt University Medical CenterVanderbilt Kennedy CenterRekrutteringAlzheimers sygdom | Downs syndrom | Downs syndrom, delvis trisomi 21Forenede Stater
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Manchester University NHS Foundation TrustRekrutteringAdrenal hyperplasi, medfødtDet Forenede Kongerige
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Medical College of WisconsinUniversity College, London; Indiana UniversityRekrutteringFunktionelle gastrointestinale lidelser | Posturalt ortostatisk takykardisyndrom | Hypermobilt Ehlers-Danlos syndrom | Autonomisk nervesystemsygdom | Ubalance i det autonome nervesystemForenede Stater
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Sixera PharmaRekrutteringNetherton syndromFrankrig
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OcugenRekrutteringRetinitis Pigmentosa | Leber medfødt amauroseForenede Stater
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University Hospital, ToulouseRekrutteringNoonans syndromFrankrig
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Imagine InstituteRWTH Aachen University; Ruhr University of Bochum; Medical University of...RekrutteringEpilepsi | Tuberøs skleroseFrankrig
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Peter MacCallum Cancer Centre, AustraliaNational Health and Medical Research Council, Australia; University of...RekrutteringHæmatologiske sygdomme | Arvelig blodpladesygdom | Arveligt BMF syndromAustralien
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Massachusetts Institute of TechnologyRekruttering
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Weill Medical College of Cornell UniversityRekrutteringTethered Cord Syndrome | Forbundet snor | Spina Bifida Occulta | Okkult Spina BifidaForenede Stater
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Tetra Discovery PartnersRekrutteringFragilt X syndromForenede Stater
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University of North Carolina, Chapel HillThe Hospital for Sick Children; Washington University School of Medicine; McGill University og andre samarbejdspartnereRekrutteringPrimær ciliær dyskinesi | Kartageners syndromForenede Stater, Canada
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Universiteit AntwerpenUniversity Hospital, AntwerpRekruttering
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Aardvark Therapeutics, Inc.Children's Hospital Colorado; Stanford UniversityRekrutteringPrader-Willi syndromForenede Stater
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Assistance Publique - Hôpitaux de ParisIkke rekrutterer endnu
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Hacettepe UniversityRekrutteringLivskvalitet | Downs syndrom | Deltagelse | AktivitetKalkun
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National Cancer Institute (NCI)Childrens Oncology Group (COG); LLS PedAL LLCRekrutteringDowns syndrom | Tilbagevendende akut myeloid leukæmi | Tilbagevendende myelodysplastisk syndrom | Refraktær akut myeloid leukæmi | Refraktært myelodysplastisk syndrom | Tilbagevendende blandet fænotype akut leukæmi | Ildfast blandet fænotype Akut leukæmi | Akut myeloid leukæmi efter cytotoksisk terapi | Myelodysplastisk syndrom efter cytotoksisk terapiForenede Stater
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Cairo UniversityIkke rekrutterer endnu
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UMC UtrechtSanquin Research & Blood Bank Divisions; National Institute for Public... og andre samarbejdspartnereRekrutteringDowns syndrom | SARS-CoV-2-vaccinationHolland
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Georgia State UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...Rekruttering
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Neurona TherapeuticsCalifornia Institute for Regenerative Medicine (CIRM)RekrutteringMesial temporallaps epilepsi med hippocampus skleroseForenede Stater
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Xinhua Hospital, Shanghai Jiao Tong University...Ikke rekrutterer endnu
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Spruce BiosciencesRekrutteringMedfødt binyrehyperplasi | 21-OHDForenede Stater
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Children's Hospital of Fudan UniversityRekruttering
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Hospices Civils de LyonRekrutteringAutismespektrumforstyrrelse | Smith-Magenis syndromFrankrig
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Medical University of GdanskRekrutteringFedme | Hyperandrogenisme | Metabolisk syndrom | Metabolisk sygdomPolen
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Darcy KruegerRekrutteringEpilepsi | Tuberøs sklerosekompleksForenede Stater
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Ain Shams UniversityRekruttering
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Adrenas Therapeutics IncRekrutteringMedfødt binyrehyperplasiForenede Stater
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University of OxfordHoffmann-La Roche; Foundation for Angelman Syndrome Therapeutics UKRekruttering
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Tasly GeneNet Pharmaceuticals Co., LtdRekrutteringCharcot-Marie-Tooth Type 1AKina
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University Hospital, Strasbourg, FranceRekruttering
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University Hospital of North NorwayRekrutteringSmerter i lænden | Mavesmerter | NervekompressionssyndromNorge
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Chunxiu GongThe First Affiliated Hospital with Nanjing Medical University; Tongji Hospital og andre samarbejdspartnereIkke rekrutterer endnuGenetiske sygdomme, medfødte | Lille til spædbørn i svangerskabsalderen | Silver-Russell syndrom
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Ohio State UniversityUniversity of HoustonRekrutteringBrydningsfejl | Downs syndromForenede Stater
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Noema Pharma AGRekrutteringTuberøs sklerosekompleksForenede Stater, Kalkun, Polen, Spanien, Det Forenede Kongerige, Indien, Italien, Israel
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Assiut UniversityIkke rekrutterer endnuVækstforstyrrelser
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University of Colorado, DenverRekrutteringTurners syndromForenede Stater
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University Hospital, MontpellierRekruttering
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Eunice Kennedy Shriver National Institute of Child...RekrutteringBØRN syndrom | Smith Lemli Opitz syndrom | Lathosterolosis | DesmosterolosisForenede Stater
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Corporacion Parc TauliInstituto de Salud Carlos IIIRekrutteringSøvnforstyrrelse | Hyperfagi | AdfærdsforstyrrelserSpanien
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University Hospital, ToulouseRekruttering
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National Heart, Lung, and Blood Institute (NHLBI)RekrutteringAlvorlig aplastisk anæmi | Telomerbiologiske lidelser | Arvelige knoglemarvssvigtsyndromerForenede Stater
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Neuren Pharmaceuticals LimitedRekruttering