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Søg i kliniske forsøg efter: Inborn errors of metabolism
I alt 431381 resultater
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Forge Biologics, IncRekrutteringKrabbes sygdomForenede Stater
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SanofiRekruttering
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Inozyme PharmaRekrutteringGeneraliseret arteriel forkalkning af spædbørn | Autosomal recessiv hypophosphatæmisk rakitt | Ectonucleotid Pyrophosphatase/phosphodiesterase1 mangelForenede Stater, Det Forenede Kongerige
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University of AberdeenIkke rekrutterer endnuKræft | Seglcellesygdom | Immunsuppression | Medfødte metabolismefejl | Organtransplantation | KOL Astma
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University Hospital Inselspital, BerneRekrutteringCerebral amyloid angiopati | Cadasil | Cerebrovaskulær sygdom i små kar | CAA - Cerebral Amyloid AngiopatiSchweiz
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Amydis Inc.National Institutes of Health (NIH); National Institute on Aging (NIA)Rekruttering
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Albina Nowak, MDIkke rekrutterer endnu
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Chiesi Farmaceutici S.p.A.ICON plcRekruttering
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRekrutteringSanfilippo syndrom | MPS3Forenede Stater
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University Medicine GreifswaldWuerzburg University Hospital; University of GöttingenRekruttering
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Mackay Memorial HospitalRekruttering
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Intellia TherapeuticsRekrutteringTransthyretin-relateret (ATTR) familiær amyloid kardiomyopati | Transthyretin-relateret (ATTR) familiær amyloid polyneuropati | Vildtype transthyretin hjerteamyloidoseDet Forenede Kongerige, New Zealand, Sverige
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Children's Hospital Medical Center, CincinnatiSanofiRekrutteringFabrys sygdomForenede Stater
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University Hospital, BordeauxRekrutteringIntellektuel handicap | Cystisk fibrose | Neurodegeneration med hjernejernakkumulation (NBIA) | Medfødt hjertefejl | Albinisme | Rubinstein-Taybi syndrom | Periventrikulær nodulær heterotopiFrankrig
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Shanton Pharma Co., Ltd.RekrutteringGigtForenede Stater, Puerto Rico
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier... og andre samarbejdspartnereRekrutteringMedfødt binyrehyperplasi | Hæmofili A | Hæmofili B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystisk fibrose | Alpha 1-Antitrypsin mangel | Seglcellesygdom | Fanconi Anæmi | Kronisk granulomatøs sygdom | Wilsons sygdom | Svær medfødt neutropeni | Ornithin Transcarbamylase mangel | Mucopolysaccharidosis VI | Lysosomal... og andre forholdBelgien
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Immusoft of CA, Inc.RekrutteringMucopolysaccharidosis IH/S | Mucopolysaccharidosis ISForenede Stater
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Novartis PharmaceuticalsRekrutteringHeterozygot eller homozygot familiær hyperkolesterolæmiHolland, Israel, Ungarn, Italien, Tyskland, Spanien, Forenede Stater, Frankrig, Norge, Den Russiske Føderation, Sydafrika, Kalkun, Det Forenede Kongerige, Canada, Schweiz, Brasilien, Libanon, Slovenien, Polen, Taiwan, Malaysia
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Leiden University Medical CenterRekruttering
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Yonsei UniversityRekrutteringFabrys sygdomKorea, Republikken
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University Children's Hospital, ZurichRekrutteringUrea cyklus lidelserSchweiz
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H. Lundbeck A/SRekrutteringMedfødt binyrehyperplasiDet Forenede Kongerige
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TakedaIkke rekrutterer endnu
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Purdue UniversityRekrutteringLaktoseintoleranceForenede Stater
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Purdue UniversityRekrutteringLaktoseintoleranceForenede Stater
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital... og andre samarbejdspartnereRekruttering
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InventisBio Co., LtdRekruttering
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National Institutes of Health Clinical Center (CC)RekrutteringMedfødt binyrehyperplasiForenede Stater
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Purdue UniversityRekrutteringLaktoseintoleranceForenede Stater
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Ionis Pharmaceuticals, Inc.RekrutteringPelizaeus-Merzbachers sygdomFrankrig, Australien, Tyskland, Holland
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Olatec Therapeutics LLCRekrutteringGigt | Ledsmerter | Gigt | Gigt Flare | Gigt arthritis | Akut gigtudbrud | GigtangrebForenede Stater, Spanien, Frankrig
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Eunice Kennedy Shriver National Institute of Child...RekrutteringNiemann-Pick sygdom type C1 | Juvenil neuronal ceroid lipofuscinose | Smith-Lemli-Opitz syndrom | Kreatin Transporter mangelForenede Stater
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Fundación Española de Hematología y HemoterapíaRekrutteringNiemann-Pick Sygdomme | Gauchers sygdom | Splenomegali | Syre SphingoMyelinase mangel | ASMDSpanien
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Institute of Health Information and Statistics...Centre of Cardiovascular and Transplantation Surgery, Czech Republic; The... og andre samarbejdspartnereRekrutteringFamiliær hyperkolesterolæmiTjekkiet
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Masonic Cancer Center, University of MinnesotaRekrutteringMucopolysaccharidosis type I | Hæmatopoietisk celletransplantationForenede Stater
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University of California, San FranciscoRekrutteringMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolmans sygdom | Pompes sygdom infantil | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopatisk Gauchers sygdomForenede Stater
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Odense University HospitalIkke rekrutterer endnuFamiliær hyperkolesterolæmiDanmark
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Lille Catholic UniversityVariant Bio, Inc.RekrutteringNyreinsufficiens, kronisk | GigtNy Kaledonien
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Assistance Publique - Hôpitaux de ParisIkke rekrutterer endnu
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Ramsay Générale de SantéEuropean Clinical Trial Experts NetworkIkke rekrutterer endnuDialyse | Jernaflejring | Iatrogen hæmosideroseFrankrig
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Rekruttering
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Eunice Kennedy Shriver National Institute of Child...RekrutteringNiemann-Pick sygdom, type CForenede Stater
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LG ChemRekrutteringHyperurikæmi | Gigt | Gigt Flare | TophiForenede Stater
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University of MinnesotaRekrutteringGauchers sygdom, type 3Forenede Stater
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LG ChemRekrutteringHyperurikæmi | Gigt | Gigt Flare | TophiForenede Stater
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BioMarin PharmaceuticalSyneos HealthRekrutteringFenylketonuri, moderTyskland, Forenede Stater, Italien
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Massachusetts General HospitalPfizer; Akcea Therapeutics; Alnylam Pharmaceuticals; Eidos Therapeutics, a...RekrutteringHjertefejl | Amyloidose | Hjertesvigt, diastolisk | Transthyretin amyloidoseForenede Stater
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University of ThessalyIkke rekrutterer endnuOxidativt stress | Kulhydratmetabolismeforstyrrelse | G6PD-mangel
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Marcello ArcaPfizer; Göteborg University; University of HelsinkiIkke rekrutterer endnuFamiliær Hypobetalipoproteinæmi | Familiær Hypobetalipoproteinæmi - heterozygot form
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRekruttering