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I alt 30413 resultater
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Hoffmann-La RocheIkke rekrutterer endnuDuchennes muskeldystrofiForenede Stater
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Lancashire Teaching Hospitals NHS Foundation TrustDuchenne UKRekruttering
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Ionis Pharmaceuticals, Inc.Ikke rekrutterer endnuMethyl CpG Binding Protein 2 (MECP2) Duplikationssyndrom
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SpinogenixAvance Clinical Pty Ltd.Ikke rekrutterer endnuFragilt X syndromForenede Stater
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Nido Biosciences, Inc.RekrutteringSpinal og Bulbar muskelatrofi | Kennedys sygdomKorea, Republikken, Danmark, Italien, Det Forenede Kongerige
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Başak Çağla ArslanHacettepe UniversityRekrutteringDuchennes muskeldystrofi | Ergoterapi | GamificationKalkun
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CSL BehringIkke rekrutterer endnu
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Peking Union Medical College HospitalIkke rekrutterer endnuDuchenne muskeldystrofi (DMD)
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Regeneron PharmaceuticalsIntellia TherapeuticsIkke rekrutterer endnu
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IRCCS Eugenio MedeaRekrutteringMuskeldystrofier | Beckers muskeldystrofi | Lembælte muskeldystrofi | Facio-Scapulo-Humeral DystrofiItalien
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Fondazione Policlinico Universitario Agostino Gemelli...RekrutteringDuchennes muskeldystrofi | Naturhistorie | Motor funktion; RetarderingItalien
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University of MalagaIkke rekrutterer endnuMuskeldystrofi | Duchennes muskeldystrofi | Beckers muskeldystrofiSpanien
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Seoul National University HospitalIkke rekrutterer endnuMuskeldystrofi, Duchenne | Øvre ekstremitet | Ortotiske enhederKorea, Republikken
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Equilibra Bioscience LLCRekrutteringHæmofili A | Hæmofili B | Sunde deltagereForenede Stater
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Rekruttering
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West China HospitalRekruttering
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRekrutteringPyruvat dehydrogenase kompleks mangelForenede Stater
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Rett Syndrome Research TrustIkke rekrutterer endnuRett syndromForenede Stater
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IRCCS San RaffaeleRekruttering
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Craig EricksonHealx LimitedRekrutteringFragilt X syndromForenede Stater
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Chiesi Farmaceutici S.p.A.ICON plcIkke rekrutterer endnu
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ENCellIkke rekrutterer endnuDuchennes muskeldystrofiKorea, Republikken
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Caroline Michaela KistorpSanofiIkke rekrutterer endnuKroniske nyresygdomme | Fabrys sygdomDanmark
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National Institute of Allergy and Infectious Diseases...RekrutteringKronisk granulomatøs sygdom (CGD) | X-forbundet kronisk granulomatøs sygdomForenede Stater
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Suzhou Alphamab Co., Ltd.RekrutteringHæmofili A med inhibitor | Hæmofili B med inhibitorKina
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IRCCS Fondazione Stella MarisRekrutteringFragilt X syndromItalien
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IRCCS Fondazione Stella MarisRekrutteringKreatinmangel, X-bundet | Kreatinmangelsyndrom på grund af Gamt-mangelItalien
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases...Ikke rekrutterer endnuMuskeldystrofi | Dyrke motion | Duchennes muskeldystrofi | Vasodilatation | DMD | Muskeldystrofi hos børn | Duchennes sygdom
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InnoVec Biotherapeutics Inc.Peking Union Medical College HospitalRekrutteringØjensygdomme | Nethindedegeneration | Nethindesygdom | RetinoschisisKina
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRekrutteringFragilt X syndromSerbien
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BioMarin PharmaceuticalRekrutteringDuchennes muskeldystrofiSpanien, Det Forenede Kongerige
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Institut National de la Santé Et de la Recherche...RekrutteringInfektioner | Autoimmune sygdomme | Diagnose | ImmundefektFrankrig, Forenede Stater, Australien, Belgien, Japan, Holland
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UniQure Biopharma B.V.RekrutteringFabrys sygdomForenede Stater
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Sarepta Therapeutics, Inc.RekrutteringDuchennes muskeldystrofiForenede Stater
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... og andre samarbejdspartnereIkke rekrutterer endnu
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... og andre samarbejdspartnereIkke rekrutterer endnuFragilt X syndrom
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRekruttering
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iECURE, Inc.RekrutteringUrea cyklus lidelser, medfødt | Ornithin Transcarbamylase mangel | Ornithin Transcarbamylase mangelsygdom | Ornithin-carbamoyltransferase-mangel (lidelse)Det Forenede Kongerige
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Hospices Civils de LyonIkke rekrutterer endnuX-Linked Hypophosphatemic Rickets
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RekrutteringAutismespektrumforstyrrelse | Autistisk lidelse | Fragilt X syndrom | Aspergers syndromForenede Stater
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University of CambridgeSanofiRekrutteringFabrys sygdom, hjertevariantDet Forenede Kongerige
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Sardocor Corp.Ikke rekrutterer endnuDMD-associeret dilateret kardiomyopati
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRekrutteringCerebral adrenoleukodystrofi (CALD)Forenede Stater
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Rocket Pharmaceuticals Inc.Rekruttering
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Children's Hospital of Fudan UniversityIkke rekrutterer endnu
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Children's Hospital of Fudan UniversityRekruttering
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Minoryx Therapeutics, S.L.RekrutteringX-bundet adrenoleukodystrofiFrankrig
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Qilu Hospital of Shandong UniversityRekrutteringFabrys sygdom | Hypertrofisk kardiomyopati | Venstre ventrikulær hypertrofiKina
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Gianni SoraruMario Negri Institute for Pharmacological ResearchRekruttering