- ICH GCP
- Registro degli studi clinici negli Stati Uniti
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Studi clinici sponsorizzati da Rare Disease Research, LLC
Totale 263 risultati
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriReclutamentoMalattia di Gaucher di tipo 1Stati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriReclutamentoGangliosidosi GM2 | Gangliosidosi GM1 | Malattia di Tay-Sachs | Malattia di Sandoff | Malattia di Tay-Sachs ad esordio tardivoStati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMucopolisaccaridosi di tipo IStati Uniti
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriTerminatoDisturbi del ciclo dell'ureaStati Uniti, Canada
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriTerminatoMalattia di Tay-Sachs | Malattia di Sandoff | Gangliosidosi GM1 | Gangliosidosi GM2Stati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMucopolisaccaridosi di tipo I | Mucopolisaccaridosi di tipo II | Mucopolisaccaridosi di tipo VI | Mucopolisaccaridosi di tipo IV | Mucopolisaccaridosi di tipo VIIStati Uniti, Canada
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University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriSconosciutoMalattia di FabriStati Uniti
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National Center for Research Resources (NCRR)Ann & Robert H Lurie Children's Hospital of ChicagoCompletatoDifetti cardiaci, congeniti | Tetralogia di Fallot | Stenosi della valvola polmonare | Ipoparatiroidismo | Atresia polmonare | Difetti cardiaci conotruncali
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National Institute of Neurological Disorders and...Harborview Injury Prevention and Research CenterCompletatoDisturbo convulsivo post-traumatico | Lesioni alla testa
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Cognivue, Inc.UH, Cleveland Medical Center; Kaweah Delta District Hospital; Riiid Research LLC; US Medical Care INCAttivo, non reclutanteDisfunzione cognitiva | Declino cognitivo | Salute del cervello | Post sindrome da CoV-2 | COVID a lungo raggioStati Uniti
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National Institute of Allergy and Infectious Diseases...The Emmes Company, LLC; US Military HIV Research ProgramCompletatoFebbre emorragica, EbolaUganda
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University of South FloridaNational Heart, Lung, and Blood Institute (NHLBI); National Institute of Arthritis... e altri collaboratoriAttivo, non reclutanteVasculite | Granulomatosi associata a poliangioite | Granulomatosi di WegenerStati Uniti
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University of CincinnatiNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD); FDA...CompletatoLinfangioleiomiomatosiStati Uniti, Canada, Giappone
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National Human Genome Research Institute (NHGRI)Therapeutics for Rare and Neglected Diseases (TRND)ReclutamentoMiopatia GNE | Malattie correlate alla GNEStati Uniti
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Artann LaboratoriesNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... e altri collaboratoriCompletatoColonscopia ambulatoriale per lo screening del cancro del colon-retto o per sintomi suggestivi di malattie del colonStati Uniti
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Centers for Disease Control and PreventionWashington University School of Medicine; The Miriam Hospital; Hennepin Healthcare... e altri collaboratoriCompletatoStudio per comprendere la storia naturale dell'HIV/AIDS nell'era della terapia efficace (studio SUN)Infezioni da HIV | Malattie trasmesse sessualmenteStati Uniti
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Andrea GropmanEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriReclutamentoMalattie cerebrali, metaboliche, congenite | Metabolismo degli aminoacidi, errori congeniti | Disturbi del ciclo dell'ureaStati Uniti, Canada, Germania, Svizzera
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French National Agency for Research on AIDS and...Merck Sharp & Dohme LLCCompletato
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French National Agency for Research on AIDS and...Merck Sharp & Dohme LLCCompletatoInfezione da HCV | Cirrosi epatica, sperimentaleFrancia
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Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminatoMalattia da carenza di ornitina transcarbamilasi
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Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)CompletatoCarenza di 21-idrossilasiStati Uniti, Brasile
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Baylor Research InstituteNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriSconosciuto
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Johns Hopkins Bloomberg School of Public HealthCenters for Disease Control and Prevention; International Rescue Committee; University...CompletatoFebbreCongo, Repubblica Democratica del
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); National Center for Advancing Translational Sciences (NCATS) e altri collaboratoriReclutamentoVasculite | Granulomatosi eosinofila con poliangioite (EGPA) | Vasculite crioglobulinemica (CV) | Vasculite indotta da farmaci | Vasculite da IgA | Vasculite cutanea isolata | Granulomatosi con poliangioite (GPA) | Poliangioite microscopica (MPA) | Poliarterite nodosa (PAN) | Vasculite orticarioideStati Uniti, Canada
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University Research Co, LLCDuke University; United States Agency for International Development (USAID); Centers... e altri collaboratoriSconosciutoMalaria, Falciparum | Diagnosi di malariaBirmania
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Wanqi ZhangShandong Institute for Endemic Disease Control and Research; Tianjin Maternal...SconosciutoCorrelati alla gravidanza | Reazione allo iodio | Overdose di composti di iodioCina
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National Center for Research Resources (NCRR)Johns Hopkins University; National Institute of Neurological Disorders and Stroke...CompletatoDolore | Fuoco di Sant'Antonio
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National Center for Research Resources (NCRR)National Institute of Neurological Disorders and Stroke (NINDS); University of...CompletatoDistrofia muscolare di Duchenne
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Pamela MunsterNovartis; Pharmacyclics LLC.; Xynomic Pharmaceuticals, Inc.; GlaxoSmithKline Research...Attivo, non reclutanteTumori solidi metastaticiStati Uniti
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State University of New York at BuffaloEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriReclutamento
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University of VirginiaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); DexCom... e altri collaboratoriCompletatoDiabete mellito, tipo 1Stati Uniti, Olanda, Francia, Italia
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French National Agency for Research on AIDS and...Merck Sharp & Dohme LLC; Gilead SciencesCompletatoInfezioni da HIV | TubercolosiCosta d'Avorio
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... e altri collaboratoriCompletatoDiscinesia ciliare primaria | Sindrome di KartagenerStati Uniti, Canada
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... e altri collaboratoriReclutamentoLinfangioleiomiomatosiStati Uniti
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Lindell WeaverU.S. Army Medical Research and Development Command; The Emmes Company, LLC; Intermountain... e altri collaboratoriCompletatoFocus: adulti sani senza lesioni cerebraliStati Uniti
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PATHInternational Centre for Diarrhoeal Disease Research, Bangladesh; The Emmes Company... e altri collaboratoriCompletatoCancro cervicaleBangladesh, Ghana
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National Institute of Allergy and Infectious Diseases...Walter Reed Army Institute of Research (WRAIR); The Emmes Company, LLC; US Military... e altri collaboratoriAttivo, non reclutante
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Weill Medical College of Cornell UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... e altri collaboratoriCompletatoMalattia di Batten | Ceroidolipofuscinosi neuronale tardiva infantileStati Uniti
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National Center for Research Resources (NCRR)University of California, Los Angeles; National Institute of Neurological Disorders...Completato
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research... e altri collaboratoriReclutamentoProteinosi alveolare polmonareStati Uniti
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI); National Center for Research... e altri collaboratoriCompletatoDiscinesia ciliare primariaStati Uniti, Canada
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National Center for Research Resources (NCRR)University of California, Los Angeles; National Institute of Neurological Disorders...CompletatoMalattia di Huntington
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Columbia UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletato
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMalattia di Niemann-Pick, tipo CStati Uniti
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University of VirginiaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); DexCom... e altri collaboratoriCompletatoDiabete mellito, tipo 1Stati Uniti
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University of California, San DiegoBaylor College of Medicine; Boston Children's Hospital; Rare Diseases Clinical... e altri collaboratoriCompletatoMalattie del sistema nervoso | Sindrome di AngelmannStati Uniti
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoDispepsiaStati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMucopolisaccaridosiStati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMorbo di Parkinson | Malattia di GaucherStati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMalattia di Tay-Sachs | Malattia di Sandoff | Malattia di Tay Sachs ad esordio tardivoStati Uniti