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Kliniske forsøg med Fragilt X Mental Retardation Syndrome
I alt 10924 resultater
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...Baylor College of MedicineAfsluttet
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University Hospital, MontpellierAgence de La BiomédecineAktiv, ikke rekrutterendeFragilt X syndrom | Huntingtons sygdom | Myotonisk dystrofi 1Frankrig
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of... og andre samarbejdspartnereRekruttering
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Jazz PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Spanien, Italien, Det Forenede Kongerige
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Center for Rare Neurological Diseases, Norcross...Ultragenyx Pharmaceutical Inc; Rett Syndrome Research TrustUkendt
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetRett syndrom | CDKL5 lidelse | MECP2 Duplikationslidelse | FOXG1 syndromForenede Stater
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National Taiwan University HospitalAfsluttetNeurologisk lidelse | Rett syndrom
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbejdspartnereAfsluttetRett syndrom | MECP2 duplikationsforstyrrelse | Rett-relateret lidelseForenede Stater
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University... og andre samarbejdspartnereRekrutteringSygdomme i nervesystemet | Neurologiske manifestationer | Neuroadfærdsmæssige manifestationer | Genetiske sygdomme, X-forbundet | Intellektuel handicap | Neuroudviklingsforstyrrelser | Neurologisk lidelse | Rett syndrom | Genetisk sygdom | Rett syndrom, atypiskForenede Stater
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Azienda Ospedaliera Universitaria SeneseEuropean Institute of Oncology; Kolfarma s.r.l. - ItalyAfsluttetEpilepsi | Livskvalitet | Dysbiose | Rett syndromItalien
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Newron Pharmaceuticals SPAAfsluttetRett syndromForenede Stater, Indien, Det Forenede Kongerige, Australien, Italien
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University of Alabama at BirminghamEunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetCDKL5 | Rett syndrom | MECP2 duplikering | FOXG1 lidelserForenede Stater
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Rett Syndrome Research TrustIkke rekrutterer endnuRett syndromForenede Stater
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Ariel UniversityAssociazione Italiana Rett (AIRETT)Ikke rekrutterer endnuRett syndromItalien
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University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute... og andre samarbejdspartnereAfsluttetRett syndrom, bevaret talevariant | Mecp2 duplikationssyndrom | Rett-relaterede lidelserForenede Stater
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Institute for Neurodegenerative DisordersAfsluttetParkinsons sygdom | Alzheimers sygdom | Mild kognitiv svækkelse | Fragilt X syndrom | Huntingtons sygdom | Autistiske Spektrum ForstyrrelserForenede Stater
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Ariel UniversityASST Santi Paolo e CarloAfsluttet
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Eunice Kennedy Shriver National Institute of Child...AfsluttetFragilt X syndrom | For tidlig ovariesvigt | For tidlig overgangsalder | FMR1 præmutation | Primær Ovairan InsufficiensForenede Stater
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Ionis Pharmaceuticals, Inc.Ikke rekrutterer endnuMethyl CpG Binding Protein 2 (MECP2) Duplikationssyndrom
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Ionis Pharmaceuticals, Inc.RekrutteringMethyl CpG Binding Protein 2 (MECP2) DuplikationssyndromForenede Stater
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Baylor College of MedicineAfsluttet
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State University of New York - Upstate Medical...AfsluttetFamiliær encefalopati med neuroserpin-inklusionskroppe | X-bundet mental retardering | Medfødt lodret talus | Idiopatisk generaliseret epilepsi | Familiær demensForenede Stater
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University of Mississippi Medical CenterAfsluttetAutistisk lidelse | Rett syndrom | Aspergers syndrom | Gennemgribende udviklingsforstyrrelse | Disintegrativ lidelse i barndommenForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetAutisme | Aspergers syndrom | Retts lidelseForenede Stater
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Janssen-Ortho Inc., CanadaAfsluttetAutistisk lidelse | Udviklingshæmning | Rett syndrom | Aspergers syndrom | DCild udviklingsforstyrrelser, gennemgående
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxLedigMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater
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National Taiwan University HospitalUkendtRett syndrom | Tourettes syndrom | Tic lidelserTaiwan
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Assistance Publique - Hôpitaux de ParisAfsluttet
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Universitaire Ziekenhuizen KU LeuvenKU LeuvenAfsluttetMeddelelse | Forældre-barn relationer | Opførsel, barnBelgien
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Baylor College of MedicineUniversity of California, San Diego; University of Alabama at Birmingham; Boston Children's Hospital og andre samarbejdspartnereAfsluttetPrader-Willi syndrom | Rett syndrom | Angelman syndrom | SøvnproblemerForenede Stater
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Kunming Hope of Health HospitalAfsluttet
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CENTOGENE GmbH RostockAfsluttetMucopolysaccharidosis II | Hunters syndrom | Jægers syndrom, mild form | Hunter's Canal SyndromeMexico
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Uskudar UniversityRekrutteringLesch-Nyhan syndromKalkun
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Rare Thyroid Therapeutics International ABVitaccess LtdAfsluttetAllan-Herndon-Dudley syndrom | Monocarboxylat Transporter 8 (MCT8) mangelDet Forenede Kongerige
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ShireAfsluttetHunters syndromForenede Stater, Spanien, Canada, Det Forenede Kongerige, Mexico, Australien, Frankrig
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Green Cross CorporationAfsluttet
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ShireAfsluttetHunters syndromForenede Stater, Det Forenede Kongerige
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Green Cross CorporationUkendtHunters syndromKorea, Republikken
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRekrutteringMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater, Det Forenede Kongerige, Holland
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TakedaRekruttering
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TakedaLedigAdgangsprogram efter undersøgelse af Idursulfase-IT sammen med Elaprase hos børn med Hunters syndromHunters syndromForenede Stater, Australien, Mexico, Spanien, Det Forenede Kongerige
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Green Cross CorporationAfsluttet
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The Catholic University of KoreaAfsluttetMetabolisk syndrom X | Metabolisk kardiovaskulært syndrom | Insulinresistenssyndrom X | Dysmetabolisk syndrom XKorea, Republikken
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Eunice Kennedy Shriver National Institute of Child...Afsluttet
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Cyprium Therapeutics, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... og andre samarbejdspartnereAfsluttetMenkes sygdom | Occipital Horn Syndrom | Uforklarlig kobbermangelForenede Stater
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ShireAfsluttetHunters syndromForenede Stater, Det Forenede Kongerige
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University Hospital, BrestUkendtDysautonomi | Maskulinitet | MECP2-relateret svær neonatal encefalopatiFrankrig
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University Hospital, ToulouseRekrutteringEpilepsi | Prader-Willi syndrom | Angelman syndrom | Smith-Magenis syndrom | X Fragilt SyndromFrankrig