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Kliniske forsøg med X-bundet trombocytopeni
I alt 4553 resultater
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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ACADIA Pharmaceuticals Inc.Afsluttet
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IRCCS Eugenio MedeaAssociazione Italiana Rett (AIRett) O.n.l.u.s.Afsluttet
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Rett Syndrome Research TrustDuke UniversityAfsluttet
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Anavex Life Sciences Corp.International Rett Syndrome Foundation Rettsyndrome.orgAfsluttet
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Montefiore Medical CenterRett Syndrome Research TrustAfsluttet
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Montefiore Medical CenterRett Syndrome Research TrustAfsluttetRett syndromForenede Stater
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Assistance Publique Hopitaux De MarseilleAfsluttet
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Medical University of ViennaAfsluttet
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases...AfsluttetHypophosphatemisk rakitt, X Linked DominantForenede Stater
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National Institute of Blood and Marrow Transplant...RekrutteringImmun trombocytopeni purpuraPakistan
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Rekruttering
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Neurogene Inc.RekrutteringRett syndromForenede Stater
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University of SienaRekruttering
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Vyant BioIkke rekrutterer endnu
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Rett Syndrome Research TrustVanderbilt University Medical CenterAfsluttetRett syndromForenede Stater
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHAfsluttetRett syndromCanada, Australien, Det Forenede Kongerige
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ACADIA Pharmaceuticals Inc.Afsluttet
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Rett Syndrome Research TrustAfsluttetRett syndromForenede Stater
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National Human Genome Research Institute (NHGRI)AfsluttetRett syndromForenede Stater
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Anagnostou, Evdokia, M.D.Unity Health Toronto; Holland Bloorview Kids Rehabilitation Hospital; Ontario...Ukendt
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Assistance Publique Hopitaux De MarseilleUkendt
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Neuren Pharmaceuticals LimitedBaylor College of Medicine; International Rett Syndrome FoundationAfsluttet
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Sheba Medical CenterUltragenyx Pharmaceutical IncUkendt
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Central Hospital, Nancy, FranceAfsluttet
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Hugo W. Moser Research Institute at Kennedy Krieger...Afsluttet
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Sheba Medical CenterUkendt
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Maastricht University Medical CenterAfsluttet
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Faculdades Metropolitanas UnidasUniversity of Sao PauloAfsluttet
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Eunice Kennedy Shriver National Institute of Child...Johns Hopkins UniversityAfsluttetRett syndrom
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Eunice Kennedy Shriver National Institute of Child...UkendtRett syndromForenede Stater
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Fujian Medical University Union HospitalThe Affiliated Hospital Of Guizhou Medical University; The Second Hospital... og andre samarbejdspartnereRekrutteringNydiagnosticeret immun trombocytopeni hos børn, førstelinjebehandlingKina
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspenderetSvær kombineret immundefektsygdom, X-bundetForenede Stater
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University of North Carolina, Chapel HillAfsluttetFragilt X syndrom | Psykose | AutismespektrumforstyrrelserForenede Stater
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Astellas Gene TherapiesAfsluttetX-bundet myotubulær myopatiForenede Stater, Frankrig, Det Forenede Kongerige, Canada, Tyskland
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University of FloridaAudentes TherapeuticsAfsluttetX-bundet myotubulær myopatiForenede Stater
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Great Ormond Street Hospital for Children NHS Foundation...UkendtX-bundet svær kombineret immundefektDet Forenede Kongerige
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Gruppo Italiano Malattie EMatologiche dell'AdultoAfsluttetVoksne patienter | Immun primær trombocytopeni | Splenektomi | TPO-mimetikItalien
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Ovid Therapeutics Inc.Afsluttet
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Sunshine Care FoundationMassachusetts General Hospital; Jose R. Reyes Memorial Medical CenterAfsluttetX-Linked Dystoni ParkinsonismeFilippinerne
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Jazz PharmaceuticalsGW PharmaceuticalsAfsluttetRett syndrom | RTTForenede Stater, Canada, Italien, Spanien, Det Forenede Kongerige, Australien
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University Children's Hospital BaselNovartis Pharmaceuticals; Stiftung zur Förderung medizinischer und biologischer... og andre samarbejdspartnereAktiv, ikke rekrutterende
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Children's Hospital of Fudan UniversityRekruttering
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Det Forenede Kongerige
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Taysha Gene Therapies, Inc.RekrutteringRett syndromForenede Stater, Canada
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Georgetown UniversityInternational Rett Syndrome Foundation Rettsyndrome.orgRekruttering
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Rett Syndrome Research TrustBaylor College of Medicine; Children's Hospital of Philadelphia; Boston Children... og andre samarbejdspartnereRekruttering
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ACADIA Pharmaceuticals Inc.AfsluttetRett syndromForenede Stater
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Edison Pharmaceuticals IncTrukket tilbage
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Anavex Life Sciences Corp.AfsluttetRett syndromAustralien, Det Forenede Kongerige