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Kliniske forsøg med X-bundet trombocytopeni
I alt 4554 resultater
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Peking Union Medical CollegeShenyang Sunshine Pharmaceutical Co., LTD.UkendtTrombocytopeni | Immun trombocytopeni | Idiopatisk trombocytopenisk purpuraKina
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First Affiliated Hospital of Suzhou Medical CollegeAfsluttetImmun trombocytopenisk purpuraKina
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David WilliamsAktiv, ikke rekrutterendeGenterapi | Alvorlig kombineret immundefekt, X-forbundetForenede Stater, Det Forenede Kongerige
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National Institute of Allergy and Infectious Diseases...UkendtX-forbundne kombinerede immundefektsygdommeForenede Stater
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National Institute of Allergy and Infectious Diseases...AfsluttetAlvorlig kombineret immundefektForenede Stater
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University Hospital, BordeauxAfsluttetImmun trombocytopenisk purpura | Trombopeni | Autoimmun trombocytopeni
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AmgenAfsluttetTrombocytopeni | Idiopatisk trombocytopenisk purpura | Trombocytopeni hos personer med immun (idiopatisk) trombocytopenisk purpura (ITP) | Trombocytopenisk purpura
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Children's Hospital of Chongqing Medical UniversityRekruttering
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Rare Thyroid Therapeutics International ABPremier Research Group plc; Egetis TherapeuticsRekrutteringMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater, Det Forenede Kongerige, Holland
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Zhongmou TherapeuticsRekrutteringX-bundet retinoschisisKina
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Shanghai General Hospital, Shanghai Jiao Tong University...Innostellar BiotherapeuticsRekrutteringX-bundet retinoschisisKina
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Beijing Tiantan HospitalRekruttering
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University of MinnesotaIkke længere tilgængeligX-bundet adrenoleukodystrofiForenede Stater
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationAfsluttetAdrenomyeloneuropati | X-bundet adrenoleukodystrofiHolland
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Institute of Hematology & Blood Diseases HospitalNovartis; The Second Hospital of Hebei Medical University; Henan Cancer Hospital og andre samarbejdspartnereAfsluttetKronisk HBV-infektion | Trombocytopeni PurpuraKina
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Great Ormond Street Hospital for Children NHS Foundation...RekrutteringAlvorlig kombineret immundefekt, X-forbundetDet Forenede Kongerige
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Baylor College of MedicineAfsluttet
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Mansoura UniversityIkke rekrutterer endnu
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Principia Biopharma, a Sanofi CompanyAktiv, ikke rekrutterendeImmun trombocytopeni | Immun trombocytopenisk purpuraForenede Stater, Australien, Bulgarien, Canada, Tjekkiet, Holland, Norge, Det Forenede Kongerige
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Assiut UniversityUkendtImmun trombocytopeni
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Zealand University HospitalOdense University Hospital; Rigshospitalet, DenmarkTrukket tilbageIdiopatisk trombocytopenisk purpuraDanmark
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Shandong UniversityChina Medical University, China; The Affiliated Hospital of the Chinese... og andre samarbejdspartnereTrukket tilbagePurpura | Idiopatisk trombocytopenisk purpuraKina
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mamdouh abdulmaksoud abdulrhmanAfsluttet
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The Hospital for Sick ChildrenAfsluttetX-bundet lymfoproliferativt syndrom type 2 (XLP-2)Canada
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IRCCS San RaffaeleFondazione TelethonRekrutteringKronisk granulomatøs sygdom X-bundet (X-CGD)Italien
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Assistance Publique - Hôpitaux de ParisBraintaleIkke rekrutterer endnuX-bundet adrenoleukodystrofi
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W... og andre samarbejdspartnereAfsluttetX-bundet adrenoleukodystrofiForenede Stater
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Shenzhen Geno-Immune Medical InstituteUkendt
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NeuroVia, Inc.Trukket tilbageX-forbundet adrenoleukodystrofiAustralien, Argentina, Det Forenede Kongerige, Colombia, Chile, Frankrig, Den Russiske Føderation, Ukraine
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AmgenAfsluttetTrombocytopeni | Idiopatisk trombocytopenisk purpura | Trombocytopeni hos personer med immun (idiopatisk) trombocytopenisk purpura (ITP) | Trombocytopenisk purpura
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Institute of Hematology & Blood Diseases Hospital...Henan Cancer Hospital; The Second Affiliated Hospital of Kunming Medical... og andre samarbejdspartnereAfsluttetImmun trombocytopenisk purpuraKina
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Applied Genetic Technologies CorpAfsluttetX-bundet retinoschisisForenede Stater
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GlaxoSmithKlineAfsluttetTrombocytopeniForenede Stater
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BloodworksUniversity of WashingtonAfsluttetPurpura, trombotisk trombocytopenisk | TTPForenede Stater
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Atsena Therapeutics Inc.RekrutteringX-bundet retinoschisisForenede Stater
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Rare Thyroid Therapeutics International ABEgetis Therapeutics; AnovoRxLedigMonocarboxylat Transporter 8 mangel | Allan-Herndon-Dudley syndromForenede Stater
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International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University... og andre samarbejdspartnereRekrutteringSygdomme i nervesystemet | Neurologiske manifestationer | Neuroadfærdsmæssige manifestationer | Genetiske sygdomme, X-forbundet | Intellektuel handicap | Neuroudviklingsforstyrrelser | Neurologisk lidelse | Rett syndrom | Genetisk sygdom | Rett syndrom, atypiskForenede Stater
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Universitair Ziekenhuis BrusselMarguerite - Marie Delacroix FoundationIkke rekrutterer endnuKlassiske lissencefalier og subkortikale båndheterotoperBelgien
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NightstaRx Ltd, a Biogen CompanyAfsluttetX-Linked Retinitis PigmentosaForenede Stater, Frankrig, Det Forenede Kongerige, Finland, Holland, Tyskland, Canada
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Edimer PharmaceuticalsAfsluttetX-forbundet hypohidrotisk ektodermal dysplasiForenede Stater
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationAfsluttetAdrenomyeloneuropati | X-bundet adrenoleukodystrofiSpanien
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationAfsluttetX-bundet adrenoleukodystrofiForenede Stater
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Seoul National University HospitalHallym University Medical CenterUkendtImmun trombocytopeni | Immun trombocytopenisk purpura | Helicobacter pyloriKorea, Republikken
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Institute of Hematology & Blood Diseases HospitalRekrutteringBindevævssygdomme | Autoantistoffer | Immun trombocytopeni (ITP) | Evans syndromKina
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Ionis Pharmaceuticals, Inc.RekrutteringMethyl CpG Binding Protein 2 (MECP2) DuplikationssyndromForenede Stater
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Eisai Inc.AfsluttetPurpura, trombocytopenisk, idiopatisk | Kronisk trombocytopeni | Akut idiopatisk trombocytopenisk purpuraHolland
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GlaxoSmithKlineAfsluttetPurpura, Trombocytopenisk, IdiopatiskForenede Stater, Frankrig, Holland, Spanien, Det Forenede Kongerige, Canada
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Edimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasi | Hypohidrotisk ektodermal dysplasiForenede Stater
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Edimer PharmaceuticalsAfsluttetX-bundet hypohidrotisk ektodermal dysplasi | Hypohidrotisk ektodermal dysplasiSpanien
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GlaxoSmithKlineAfsluttetPurpura, Trombocytopenisk, IdiopatiskForenede Stater