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Studi clinici sponsorizzati da Myasthenia Gravis Rare Disease Network
Totale 87 risultati
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Myasthenia Gravis Rare Disease NetworkReclutamentoMiastenia grave | MUSCHIO Miastenia Gravis | MusK MGStati Uniti
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Huashan HospitalChina Alliance for Rare Diseases; National Center for Neurological Disorders... e altri collaboratoriReclutamento
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkSconosciutoSindromi mielodisplastiche | Porpora, Trombocitopenica | Anemia, aplastica | Aplasia eritrocitaria, pura | Sindromi da insufficienza del midollo osseo | Emoglobinuria, parossistica | Leucemia, linfocitariaStati Uniti
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkSconosciutoAnemia, aplasticaStati Uniti
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkSconosciutoSindrome mielodisplasicaStati Uniti
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University of California, Los AngelesRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletatoMalattie cerebellari | Sindrome da atassia episodicaStati Uniti, Canada, Regno Unito
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Assistance Publique - Hôpitaux de ParisFrench rare diseases Healthcare Network; The French Foundation for Rare DiseasesAttivo, non reclutanteAmelogenesi imperfetta | Dentinogenesi imperfetta | Anomalie della dentinaFrancia
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletatoDisturbi miotonici | Miotonia congenita | Miotonie non distroficheCanada, Stati Uniti, Regno Unito
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletatoDisturbi del ciclo dell'urea, congeniti | Disturbo del ciclo dell'urea | Aciduria Argininosuccinica | Deficit di Argininosuccinato LiasiStati Uniti
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University of RochesterNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... e altri collaboratoriCompletatoSindrome di Andersen-Tawil | Sindrome di AndersenStati Uniti, Canada, Italia, Regno Unito
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University of California, DavisPediatric Emergency Care Applied Research NetworkReclutamentoLesioni cerebrali | Emorragie intracraniche | Danno assonale diffuso | Ferita alla testa | Fratture del cranio | Trauma cranico | Lesione cerebrale traumatica lieve | Lesioni cerebrali, acute | Lesione alla testa con emorragia intracranica | Lesione cerebrale traumatica focale con perdita di coscienzaStati Uniti
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriReclutamentoArterite a cellule giganti | Poliangioite microscopica | Poliarterite nodosa | Arterite di Takayasu | Granulomatosi eosinofila con poliangioite (Churg-Strauss) | Granulomatosi con poliangioite (di Wegener)Stati Uniti, Canada, Tacchino
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of Rare Diseases...CompletatoArterite a cellule giganti | Arterite di TakayasuStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoGranulomatosi di WegenerStati Uniti
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoArterite temporaleStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoDeterminazione dei biomarcatori dell'attività della malattia negli individui con poliarterite nodosaPoliarterite nodosaStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoProtocollo longitudinale per granulomatosi con poliangioite (di Wegener) e poliangioite microscopicaPoliangioite microscopica | Granulomatosi associata a poliangioite | Di WegenerStati Uniti, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoArterite di TakayasuStati Uniti, Canada
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... e altri collaboratoriTerminatoSindrome di Andersen-TawilStati Uniti
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS); Rare Diseases Clinical Research Network e altri collaboratoriCompletatoArterite di TakayasuStati Uniti, Canada
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... e altri collaboratoriCompletatoMalattie cerebrali, metaboliche, congenite | Deficit di ornitina transcarbamilasi | Disturbo del ciclo dell'ureaStati Uniti
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University of South FloridaNational Institutes of Health (NIH); Rare Diseases Clinical Research NetworkCompletatoOsteogenesi imperfetta | Disturbi delle ossa fragiliStati Uniti
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University of South FloridaNational Institutes of Health (NIH); Rare Diseases Clinical Research NetworkCompletatoOsteogenesi imperfetta | Disturbi delle ossa fragiliStati Uniti
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University Hospital, LilleFAI²R (Auto-immune and auto-inflammatory rare diseases French network)TerminatoCovid19 | Reumatismo infiammatorio | Malattia autoimmune sistemica | Malattie autoinfiammatorieFrancia
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University Hospital, LilleFAI²R (Auto-immune and auto-inflammatory rare diseases French network)SconosciutoMalattie autoimmuni | SARS-CoV-2 | Reumatismo infiammatorio cronicoFrancia
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... e altri collaboratoriCompletatoProtoporfiria eritropoietica | PPE | XLP | Protoporfiria legata all'X | XLPP | Protoporfiria eritropoietica dominante legata all'X | XLEPP | XLDPStati Uniti
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University of ManitobaCanadian Primary Care Sentinel Surveillance Network; Canadians Seeking Solutions... e altri collaboratoriReclutamentoMalattia renale cronicaCanada
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriCompletatoObesità | Sindrome di Prader-WilliStati Uniti
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Hospital Universitari Vall d'Hebron Research InstituteERN-EuroBloodNet (European Reference Network on Rare Hematological DiseasesReclutamentoLeucemia | Anemia | Disturbi del metabolismo del ferro | Anemia, anemia falciforme | Talassemia | Disturbo della coagulazione | Mieloma | Neoplasia linfoide | Cancro del sangue | Insufficienza del midollo osseo | Anomalie della membrana dei globuli rossi e degli enzimi | Mieloma malignoSpagna
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletatoIstiocitosi polmonare a cellule di LangerhansStati Uniti
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletatoSindrome di Birt-Hogg-DubeStati Uniti
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...Iscrizione su invitoMalattia granulomatosa, cronicaStati Uniti, Canada
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletatoSindrome di Wiskott-AldrichStati Uniti, Canada
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Assistance Publique - Hôpitaux de ParisFAI²R (Auto-immune and auto-inflammatory rare diseases French network)Non ancora reclutamentoMalattie autoimmuni | Malattie Rare | Infezione da SARS-CoV2 | Reumatismo infiammatorio cronicoFrancia
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...ReclutamentoMalattia da carenza di complesso di piruvato deidrogenasiStati Uniti
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Children's Hospital Medical Center, CincinnatiNational Center for Research Resources (NCRR); Rare Diseases Clinical Research...CompletatoProteinosi alveolare polmonareStati Uniti, Germania, Italia, Giappone
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Daniel Nishijima, MD, MASPediatric Emergency Care Applied Research NetworkCompletatoFerite e lesioni | Lesioni cerebrali | EmorragiaStati Uniti
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Daniel Nishijima, MD, MASPediatric Emergency Care Applied Research NetworkNon ancora reclutamentoEmorragia | Lesioni cerebrali, traumatiche | Lesione traumatica | Ferite e lesioni
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriReclutamentoMalattia di Gaucher di tipo 1Stati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriReclutamentoGangliosidosi GM2 | Gangliosidosi GM1 | Malattia di Tay-Sachs | Malattia di Sandoff | Malattia di Tay-Sachs ad esordio tardivoStati Uniti
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EusaPharma (UK) LimitedUniversity of Sheffield (ScHARR); KMC Health Care; Castleman Disease Collaborative...Non ancora reclutamentoMalattia di Castleman multicentrica idiopatica
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMucopolisaccaridosi di tipo IStati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriTerminatoMalattia di Tay-Sachs | Malattia di Sandoff | Gangliosidosi GM1 | Gangliosidosi GM2Stati Uniti
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletatoMucopolisaccaridosi di tipo I | Mucopolisaccaridosi di tipo II | Mucopolisaccaridosi di tipo VI | Mucopolisaccaridosi di tipo IV | Mucopolisaccaridosi di tipo VIIStati Uniti, Canada
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University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriSconosciutoMalattia di FabriStati Uniti
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriCompletatoMetabolismo degli aminoacidi, errori congeniti | Disturbi del ciclo dell'urea | Aciduria ArgininosuccinicaStati Uniti
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Children's Hospital Medical Center, CincinnatiRare Diseases Clinical Research Network; National Center for Advancing Translational...CompletatoProteinosi alveolare polmonare autoimmuneStati Uniti
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletatoProteinosi alveolare polmonare autoimmuneStati Uniti
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Icahn School of Medicine at Mount SinaiEunice Kennedy Shriver National Institute of Child Health and Human Development... e altri collaboratoriCompletatoSindrome da eccesso apparente di mineralcorticoidiStati Uniti, Brasile, Francia
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... e altri collaboratoriCompletato