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Kliniske forsøg med MPS VI
I alt 681 resultater
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Sigilon Therapeutics, Inc.Trukket tilbageMPS I | MPS1-S | MPS1-HSBrasilien, Det Forenede Kongerige
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University of LeipzigDeutsche Krebshilfe e.V., Bonn (Germany)RekrutteringMDS | MDS/MPNTyskland, Østrig
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Michael SavonaIncyte Corporation; Astex Pharmaceuticals, Inc.; TheradexRekruttering
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DKMS gemeinnützige GmbHRekrutteringAML | MDS | Perifer blodstamcelletransplantation | Graft vs værtssygdom | CMML | MDS/MPNTyskland
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Hospital de Clinicas de Porto AlegreThe Isaac FoundationAktiv, ikke rekrutterendeMucopolysaccharidoser | Mucopolysaccharidosis VI | Morquio A syndrom | Mucopolysaccharidosis IV A | MPS IV A | MPS VI | MPS - Mucopolysaccharidosis | Morquio syndrom A | Morquio syndromBrasilien
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University of California, San FranciscoRekrutteringMPS IVA | MPS VIForenede Stater
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The First Affiliated Hospital with Nanjing Medical...Jiangbin Hospital Affiliated to Jiangsu University; Nanjing Second Hospital og andre samarbejdspartnereRekruttering
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetKrabbes sygdom | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)Forenede Stater
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Peking University People's HospitalRekrutteringAkut leukæmi | MDS | CML | MDS/MPNKina
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University of California, San FranciscoDuke UniversityRekrutteringWolmans sygdom | MPS IVA | Pompes sygdom infantil | Gauchers sygdom, type 2 | MPS VI | MPS I | Gauchers sygdom, type 3 | MPS II | Mps VIIForenede Stater
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalAfsluttetMPS IVA | Maroteaux Lamy syndrom | MPS VI | Morquio syndrom AForenede Stater
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BioMarin PharmaceuticalAfsluttetMucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy syndrom)Forenede Stater, Frankrig, Australien, Tyskland, Irland, Østrig, Belgien, Italien, Litauen, Holland, Portugal, Sverige, Det Forenede Kongerige
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BioMarin PharmaceuticalAfsluttetMPS VIForenede Stater, Australien, Frankrig, Brasilien, Tyskland, Portugal, Det Forenede Kongerige
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Benjamin TomlinsonRekrutteringMyelodysplastiske syndromer | MDS/MPN Crossover syndromerForenede Stater
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Gwynn Long, M.D.ADC Therapeutics S.A.AfsluttetAkut myeloid leukæmi (AML) | Myelodysplastisk syndrom (MDS) | Myeloproliferativ neoplasma (MDS/MPN)Forenede Stater
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Children's Hospital of Eastern OntarioAfsluttet
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ShireAfsluttetMucopolysaccharidosis (MPS)Det Forenede Kongerige, Holland
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Jacqueline Garcia, MDNational Institutes of Health (NIH)RekrutteringAkut myeloid leukæmi (AML) | Kronisk myelomonocytisk leukæmi (CMML) | Myelodysplastisk syndrom (MDS) | Hæmatopoietisk stamcelletransplantation | MDS/Myeloproliferativ Neoplasma-uklassificerbar (MDS/MPN-uklassificerbar)Forenede Stater
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Assiut UniversityUkendt
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Groupe Francophone des MyelodysplasiesNovartisUkendt
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CelgeneRekrutteringBeta-thalassæmi | Myelodysplastiske syndromer (MDS) | Myeloproliferativ neoplasma (MPN)-associeret myelofibroseForenede Stater, Japan, Det Forenede Kongerige, Kalkun, Grækenland, Frankrig, Australien, Belgien, Bulgarien, Canada, Tyskland, Israel, Italien, Malaysia, Spanien, Sverige, Taiwan, Thailand, Tunesien, Libanon, Kina, Holland
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Ultragenyx Pharmaceutical IncPRA Health SciencesRekrutteringSly Syndrom | Mucopolysaccharidosis VII | MPS VII | MPS 7Forenede Stater, Tyskland, Brasilien, Argentina, Frankrig, Holland, Portugal, Spanien, Kalkun
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Ultragenyx Pharmaceutical IncAfsluttetMucopolysaccharidosis | Sly Syndrom | MPS VII | MPS 7Forenede Stater
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Alexion PharmaceuticalsAfsluttetMucopolysaccharidosis III, Type B (MPS IIIB) | Sanfilippo BDet Forenede Kongerige
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Alexion PharmaceuticalsAfsluttetMPS IIIB (Sanfilippo B syndrom)Det Forenede Kongerige
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Stanford UniversityNational Institutes of Health (NIH)AfsluttetMyelodysplastiske syndromer | Myeloproliferative lidelser | Myelodysplastiske syndromer (MDS) | Blod- og marvtransplantation (BMT) | Myeloproliferative lidelser (MPD)Forenede Stater
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Zhejiang Provincial Hospital of TCMUkendt
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Swedish Orphan BiovitrumAfsluttetSanfilippo syndrom type A (MPS IIIA)Forenede Stater, Kalkun
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Swedish Orphan BiovitrumAfsluttetSanfilippo syndrom type A (MPS IIIA)Forenede Stater, Tyskland, Kalkun
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University Hospital TuebingenRekruttering
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Montefiore Medical CenterRekrutteringAML | MDSForenede Stater
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The Second Hospital of Shandong UniversityIkke rekrutterer endnu
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Groupe Francophone des MyelodysplasiesAstex Pharmaceuticals, Inc.Aktiv, ikke rekrutterende
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Boehringer IngelheimIkke rekrutterer endnuAvanceret blødt vævssarkom | Udifferentieret Pleomorphic Sarcoma (UPS) | Myxofibrosarkom (MFS)
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Rigshospitalet, DenmarkRekruttering
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GWT-TUD GmbHRekruttering
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M.D. Anderson Cancer CenterRekruttering
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University of FlorenceAktiv, ikke rekrutterende
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PhenoSolve, LLCJacobi Medical Center; Boston Clinical TrialsAfsluttet
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Northwest Women's and Children's Hospital, Xi'an...Ukendt
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Assiut UniversityIkke rekrutterer endnu
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Tehran University of Medical SciencesUkendtKvinder med PMSIran, Islamisk Republik
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Allievex CorporationAfsluttetMucopolysaccharidosis Type IIIB | Mucopolysaccharidosis Type 3 B | MPS III B | MPS 3 BForenede Stater, Spanien, Kalkun, Taiwan, Australien, Colombia, Tyskland, Det Forenede Kongerige
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Novartis PharmaceuticalsAfsluttetPatienter, der med succes afslutter den 12-måneders behandlingsperiode i kernestudiet (de Novo Heart-modtagere), som var interesserede i at blive behandlet med EC-MPS
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Astellas Pharma Global Development, Inc.Basilea Pharmaceutica International LtdAfsluttetSunde emner | Isavuconazols farmakokinetik | Farmakokinetik af plasmamycophenolsyre (MPA) | Farmakokinetik af plasmaphenolisk glukuronid af MPA (MPAG)Forenede Stater
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Shalvata Mental Health CenterAfsluttetMPH Indflydelse på kreativitet
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Duke UniversityAfsluttet
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Memorial Sloan Kettering Cancer CenterRekrutteringMinimalt invasiv kirurgi (MIS) hysterektomiForenede Stater
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Masonic Cancer Center, University of MinnesotaTrukket tilbageMucopolysaccharidosis Type IH | Mucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome) | MPS IH, Hurler syndrom
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Center for International Blood and Marrow Transplant...Cellular Dynamics International, Inc. - A FUJIFILM CompanyAfsluttetiPS Cell Manufacturing and Banking