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Prove cliniche su Porphyria%2C+Erythropoietic
Totale 87 risultati
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Brigham and Women's HospitalCompletato
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Icahn School of Medicine at Mount SinaiReclutamento
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The University of Texas Medical Branch, GalvestonTerminatoCoproporfiria ereditaria | Porfiria acuta intermittente | Porfiria variegataStati Uniti
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University of Alabama at BirminghamPorphyria Rare Disease Clinical Research ConsortiumCompletatoProtoporfiria eritropoietica (EPP)Stati Uniti
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The University of Texas Medical Branch, GalvestonCompletatoPorfirie acuteStati Uniti
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University of Texas Southwestern Medical CenterNovartis PharmaceuticalsCompletatoPorfiria Cutanea TardaStati Uniti
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Alnylam PharmaceuticalsTerminatoPorfiria epatica acuta | Porfiria acuta intermittente (AIP) | Coproporfiria ereditaria (HCP) | Porfiria variegata (VP) | Porfiria carente di ALA deidratasi (ADP) | Porfirie epatiche | Porfiria acutaStati Uniti
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University of California, San FranciscoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... e altri collaboratoriCompletatoPorfiria acuta intermittente (AIP) | Coproporfiria ereditaria (HCP) | Porfiria variegata (VP)Stati Uniti
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Alnylam PharmaceuticalsCompletatoPorfiria acuta intermittenteStati Uniti, Regno Unito, Svezia
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Zymenex A/SCompletato
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Clinuvel (UK) Ltd.Completato
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Alnylam PharmaceuticalsNon più disponibilePorfiria epatica acuta
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Icahn School of Medicine at Mount SinaiReclutamentoPorfiria acuta intermittente (AIP)Stati Uniti
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Nordlandssykehuset HFUniversity of Oslo; Norwegian University of Science and Technology; The University... e altri collaboratoriReclutamentoPorfiria, acuta intermittenteNorvegia
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Alnylam PharmaceuticalsCompletatoPorfiria acuta intermittenteStati Uniti, Regno Unito, Svezia
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletatoPorfiria acuta intermittenteSpagna
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.CompletatoPorfiria acuta intermittenteSpagna
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The University of Texas Medical Branch, GalvestonAttivo, non reclutanteCoproporfiria ereditaria | Porfiria acuta intermittente | Porfiria variegataStati Uniti
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University of South FloridaUniversity of Miami; University of Alabama at Birmingham; Icahn School of Medicine... e altri collaboratoriCompletato
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Association pour la Recherche en Medecine InterneNon ancora reclutamentoPorfiria epatica acuta
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Alnylam PharmaceuticalsReclutamentoPorfiria epatica acutaBelgio, Francia, Germania, Regno Unito, Stati Uniti, Italia, Svezia
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Alnylam PharmaceuticalsCompletatoPorfiria, acuta intermittente | Porfiria acuta intermittente (AIP) | Porfiria epatica acuta (AHP) | Porfiria acutaSvezia
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University Hospital, Strasbourg, FranceCompletatoPorfiria Cutanea Tarda
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Alnylam PharmaceuticalsCompletatoPorfiria epatica acutaStati Uniti, Belgio, Bulgaria, Francia, Italia, Messico, Spagna, Taiwan, Regno Unito, Olanda, Corea, Repubblica di, Svizzera, Cechia, Polonia, Finlandia, Australia, Germania, Israele, Norvegia, Sud Africa
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Alnylam PharmaceuticalsCompletatoPorfiria epatica acuta | Porfiria acuta intermittente | Porfiria, acuta intermittente | Porfiria acuta | Coproporfiria ereditaria (HCP) | Porfiria variegata (VP) | Porfiria carente di ALA deidratasi (ADP)Stati Uniti, Spagna, Regno Unito, Corea, Repubblica di, Australia, Bulgaria, Canada, Danimarca, Finlandia, Francia, Germania, Italia, Giappone, Messico, Olanda, Polonia, Svezia, Taiwan
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The University of Texas Medical Branch, GalvestonCompletatoPorfiria Cutanea TardaStati Uniti
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Assistance Publique - Hôpitaux de ParisAssociation pour l'Etude des Fonctions Digestives (AEFD)SconosciutoPorfiria Cutanea TardaFrancia
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National Center for Research Resources (NCRR)University of TexasCompletato
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National Institute of Cardiology, Warsaw, PolandInstitute of Hematology and Transfusion Medicine, WarsawCompletatoPorfirie, epatichePolonia
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Nordlandssykehuset HFThe Royal Norwegian Ministry of HealthAttivo, non reclutantePorfiria acuta intermittenteNorvegia
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National Center for Research Resources (NCRR)University of TexasCompletato
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National Center for Research Resources (NCRR)University of TexasCompletato
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National Center for Research Resources (NCRR)University of TexasCompletato
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National Center for Research Resources (NCRR)University of TexasCompletato
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National Center for Research Resources (NCRR)University of TexasSconosciuto
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National Center for Research Resources (NCRR)University of TexasCompletato
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National Center for Research Resources (NCRR)University of TexasCompletato
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Wake Forest University Health SciencesNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Gilead... e altri collaboratoriCompletato
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Vanderbilt University Medical CenterReclutamentoSindrome da tachicardia ortostatica posturale | Porfiria epatica acutaStati Uniti
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Mitsubishi Tanabe Pharma America Inc.CompletatoProtoporfiria eritropoietica (EPP)Stati Uniti
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Fundación Grupo de Investigación en Cuidados Intensivos...Recordati Rare DiseasesAttivo, non reclutante
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University of UtahNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... e altri collaboratoriTerminatoProtoporfiria eritropoietica (EPP) | Protoporfiria eritropoietica legata all'XStati Uniti
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Clinuvel Europe LimitedReclutamento
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Disc Medicine, IncIscrizione su invitoProtoporfiria eritropoieticaStati Uniti, Australia
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Clinuvel Pharmaceuticals LimitedCompletatoProtoporfiria eritropoietica
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Bispebjerg HospitalCompletatoProtoporfiria eritropoieticaDanimarca
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Amy K. Dickey, M.D.Wake Forest University Health Sciences; University of TexasReclutamentoProtoporfiria eritropoietica | Protoporfiria legata all'XStati Uniti
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FDA Office of Orphan Products DevelopmentSt. Luke's-Roosevelt Hospital CenterCompletatoProtoporfiria eritropoietica
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Disc Medicine, IncAttivo, non reclutanteProtoporfiria eritropoieticaStati Uniti
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Clinuvel Pharmaceuticals LimitedCompletatoProtoporfiria eritropoieticaOlanda, Finlandia, Francia, Germania, Irlanda, Regno Unito