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Kliniske forsøg med alfa-thalassæmi
I alt 625 resultater
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CSL BehringAfsluttetCystisk fibroseBulgarien, Ungarn, Polen, Det Forenede Kongerige
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National Heart, Lung, and Blood Institute (NHLBI)Tilmelding efter invitationSeglcelleanæmi | Segl Beta Thalassæmi | Seglcelle-thalassæmi | Segl Beta Zero Thalassæmi | Seglcellesmerter | Hbss | Hbsc | Seglcelle syndrom variantForenede Stater
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Zymenex A/SEuropean CommissionAfsluttet
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Vifor (International) Inc.Labcorp Corporation of America Holdings, IncAfsluttetBeta-thalassæmi | Ikke-transfusionsafhængig thalassæmiGrækenland, Israel, Italien, Libanon, Thailand
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Arog Pharmaceuticals, Inc.LedigFLT3-ITD mutation | FLT3/TKD-mutation | PDGFR-Alpha D842V | PDGFRA-genamplifikationItalien
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Vanderbilt University Medical CenterMedical College of Wisconsin; VersitiAfsluttetSeglcelleanæmi (HbSS eller HbSβ-thalassæmi0)Forenede Stater
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Washington University School of MedicineNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) og andre samarbejdspartnereAfsluttetLevercirrhose | Alpha-1-antitrypsin mangelForenede Stater
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Shanghai First Maternity and Infant HospitalUkendt
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Alnylam PharmaceuticalsAfsluttetZZ Type Alpha-1 Antitrypsin-mangel leversygdomDet Forenede Kongerige
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Rambam Health Care CampusHadassah Medical Organization; Tel-Aviv Sourasky Medical Center; Soroka University...AfsluttetGVHD | Knoglemarvstransplantationsfejl | Alpha 1-AntitrypsinIsrael
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)AfsluttetAlpha 1 Antitrypsin mangel | AATDForenede Stater
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Aktiv, ikke rekrutterendePortal hypertension | Kolestase | Leverfibrose | Biliær atresi | Alagille syndrom | Alpha1 Anti-Trypsin mangelForenede Stater, Canada
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Chinese University of Hong KongRekrutteringHæmoglobin Barts HydropsHong Kong
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Shanghai BDgene Co., Ltd.Rekruttering
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Shenzhen HemogenRekruttering
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Assistance Publique Hopitaux De MarseilleAfsluttetThalassæmi Major (TM) | Thalassæmi Intermedia (TI) | Mikropartikler (MP) der stammer fra blodplader, endotelceller og monocytterFrankrig
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Kind Pharmaceuticals LLCIkke rekrutterer endnu
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Institute of Hematology & Blood Diseases Hospital...Shanghai Vitalgen BioPharma Co., Ltd.RekrutteringMajor Thalassæmi | Thalassæmi, BetaKina
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Shenzhen HemogenRekruttering
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Children's Hospital KarachiAfsluttet
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Dr.Saqib Hussain AnsariUkendtThalassæmi, BetaPakistan
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Shanghai BDgene Co., Ltd.Shanghai Children's Medical CenterRekruttering
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital... og andre samarbejdspartnereTilmelding efter invitation
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Imara, Inc.Afsluttetβ ThalassæmiIsrael, Frankrig, Malaysia, Kalkun, Danmark, Georgien, Grækenland, Italien, Libanon, Marokko, Holland, Tunesien, Det Forenede Kongerige
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Acceleron Pharma Inc. (a wholly owned subsidiary...AfsluttetB-thalassæmiItalien, Grækenland
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Shanghai BDgene Co., Ltd.Ruijin HospitalRekruttering
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Aga Khan UniversityAfsluttetBeta-thalassæmi major
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China Medical University HospitalAfsluttet
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Institute of Hematology & Blood Diseases HospitalR&D Kanglin BiotechRekrutteringTransfusionsafhængig beta-thalassæmiKina
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First Affiliated Hospital of Guangxi Medical UniversityGenmedicn Biopharma Ltd.RekrutteringTransfusionsafhængig beta-thalassæmiKina
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Prothya BiosolutionsAfsluttet
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EmeraMedAfsluttetBeta-thalassæmi majorAlbanien
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Tanta UniversityAfsluttetBeta-thalassæmi majorEgypten
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Nanfang Hospital of Southern Medical UniversityGuangdong Yike Gene Science and Technology CO.,LtdUkendtBeta-thalassæmi majorKina
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Novartis PharmaceuticalsTrukket tilbage
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Ain Shams UniversityUkendtBeta-thalassæmi majorEgypten
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Boston UniversityHemaQuest Pharmaceuticals Inc.AfsluttetBeta Thalassæmi IntermediaLibanon
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University of British ColumbiaAfsluttetSeglcellesygdom | Beta-thalassæmi | Seglcelleegenskab | Seglcelle-beta-thalassæmi | Seglcelle-SS sygdomCanada, Nepal
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CorrectSequence Therapeutics Co., LtdRekrutteringBeta-thalassæmi majorKina
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint...Afsluttet
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Bioray LaboratoriesPLA 923 HospitalAfsluttet
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bluebird bioAfsluttetβ-thalassæmi MajorForenede Stater, Australien, Thailand
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First Affiliated Hospital of Guangxi Medical UniversityUkendt
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Boston UniversityMahidol UniversityAfsluttetBeta Thalassæmi IntermediaThailand
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Protagonist Therapeutics, Inc.Afsluttetβ-thalassæmi | Ineffektiv erytropoieseMalaysia, Thailand, Forenede Stater, Grækenland, Det Forenede Kongerige, Kalkun, Libanon, Tunesien
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Ikke rekrutterer endnuTransfusionsafhængig beta-thalassæmiKina
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Institute of Hematology & Blood Diseases Hospital...Kanglin BiotechRekrutteringTransfusionsafhængig beta-thalassæmiKina
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bluebird bioAktiv, ikke rekrutterendeTransfusionsafhængig beta-thalassæmiForenede Stater, Frankrig, Det Forenede Kongerige, Australien, Thailand, Italien, Tyskland, Grækenland